Article 68W8B Girl with deadly inherited condition is cured with gene therapy on NHS

Girl with deadly inherited condition is cured with gene therapy on NHS

by
Andrew Gregory Health editor
from Science | The Guardian on (#68W8B)

Teddi Shaw, from Northumberland, first recipient on health service of Libmeldy, world's most expensive drug

A girl born with a rare and deadly genetic condition is expected to live a long and normal life after becoming the first person to be cured on the NHS with the help of a revolutionary gene therapy.

Teddi Shaw was diagnosed with metachromatic leukodystrophy (MLD), an inherited condition that causes catastrophic damage to the nervous system and organs. Those affected usually die young.

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