Doctors hail breakthrough in muscular dystrophy treatment
by Ian Sample Science editor from on (#3XTF2)
Researchers use experimental gene-editing procedure to correct dystrophin gene mutations in dogs
Doctors in the US have raised hopes of a treatment for muscular dystrophy, the most common fatal genetic condition in children, after mending mutations that cause the disease in dogs.
The landmark study is the first to claim success at treating the muscle wasting disorder in large mammals, though scientists on the team caution that more work lies ahead to ensure the procedure is safe and effective for use in people.
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